日期: 2009
系所: 醫學研究所
題名:
Early treatment with alglucosidase alpha prolongs long-term survival of infants with Pompe disease.
作者: Priya S. Kishnani, Deya Corzo, Nancy D. Leslie, Daniel Gruskin, Ans Van Der Ploeg, John P. Clancy, Rosella Parini, Gilles Morin, Michael Beck, Mislen S. Bauer, Mikael Jokic, Chen-En Tsai, Brian W. H. Tsai, Claire Morgan, Tara O’Meara, Susan Richards, Elisa C. Tsao, Hanna Mandel.